Huntingtin Haplotypes Provide Prioritized Target Panels for Allele-specific Silencing in Huntington Disease Patients of European Ancestry
Huntingtin Haplotypes Provide Prioritized Target Panels for Allele-specific Silencing in Huntington Disease Patients of European Ancestry
Molecular Therapy 23,
1759 (November 2015). doi:10.1038/mt.2015.128
Authors: Chris Kay, Jennifer A Collins, Niels H Skotte, Amber L Southwell, Simon C Warby, Nicholas S Caron, Crystal N Doty, Betty Nguyen, Annamaria Griguoli, Colin J Ross, Ferdinando Squitieri & Michael R Hayden
Source: Molecular Therapy - Category: Genetics & Stem Cells Authors: Chris KayJennifer A CollinsNiels H SkotteAmber L SouthwellSimon C WarbyNicholas S CaronCrystal N DotyBetty NguyenAnnamaria GriguoliColin J RossFerdinando SquitieriMichael R Hayden Source Type: research
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